top of page
Transforming drug discovery and development by designing, manufacturing, and testing the most powerful RNA Therapeutic technology
Brain Delivery
Brain-penetrant Nanoligomers can be delivered to various brain sections.
High Specificity
Low nanomolar
(~3.4 nM) dissociation constant (KD)
High Safety & Bioavailability
Large and small animal studies completed
Multiple Administration routes
First oral RNA therapeutic with brain delivery. Other routes include intranasal, injectable, intravenous.
Loss of function
Translational or transcriptional repression
High-throughput & Scale
>100 targets per run
Gram to Kg scale synthesis
Rapid hit to lead optimization
Days time scale from design to testing
Subscribe to Our Newsletter
bottom of page